Molecular Engine + Treatment
FOLFIRINOX Metastatic PROVEN
OS 11.1 vs 6.8mo gemcitabine. Standard fit metastatic.
Conroy 2011 NEJM
Gem+Nab-Paclitaxel PROVEN
OS 8.5 vs 6.7mo. Alternative or less fit.
Von Hoff 2013 NEJM
Olaparib BRCA POLO PROVEN
BRCA germline PDAC. PFS 7.4 vs 3.8mo maintenance.
Golan 2019 NEJM POLO
MSI-H → Pembrolizumab OPEN
Only 1% PDAC MSI-H. 100% checkpoint-sensitive. Screen all.
Le 2017 Science
KRAS G12D Inhibitors OPEN
MRTX1133 Phase I. Higher primary resistance than NSCLC G12C.
Fell 2020 J Med Chem